World's most expensive medicine treats infants with genetic disorder - BBC News

People at Malaysia make app for public donation people and make money 2 million dolar🎉

I think it’s an amazing time in medicine to have access to gene editing therapies in treating rare conditions. I can’t help but worry that some of these treatments are so unaffordable to the vast majority of people, and even if people can “afford” the treatment, they’re probably going to be forced in a massive financial deficit for it. While I understand that research is expensive and manufacturing of the medications is also expensive, there has to be some line to be drawn to cap costs for the sake of the patient, not to mention any role insurance may or may not play in paying. Access to lifesaving medications should be a right without the consequence of financial ruin, at what point can/should the government step in when it comes to something like this in the same way things like dialysis can be covered as life-saving and wildy expensive.

misi rakyat hadir🙏🏻 road to 9millions! ayuh rakyat Malaysia Kita Bantu

The high cost of drug therapy for genetic diseases presents a complex issue that requires thorough consideration. The development and production of these drugs does require significant investment, research, and resources. On the other hand, the high cost of these drugs can pose a significant burden or barrier for patients and families, particularly for those without adequate insurance coverage or financial resources. Such cost may prevent those who cannot afford certain drug therapies from receiving the care they need. As a result, we sometimes see that treatable diseases end up being a death sentence for some. This violates the ethical principle of distributive justice, which emphasizes the fair allocation of limited healthcare resources. In this situation, we may see a disparity in equitable access to care. Another ethical consideration is the principle of beneficence, which emphasizes protection of the well-being of patients. The high cost may limit access to care and prevent patients from receiving the treatment they need to improve their health and quality of life. Lastly, the principle of autonomy is also relevant, as patients with genetic diseases have the right to make informed decisions about their care and treatment options. However, the high cost of drug therapy may limit their ability to exercise this autonomy and make decisions based on their personal values and preferences. We must find a balance between the costs of drug therapy and the ethical principles of distributive justice, beneficence, and autonomy. This may involve developing alternative payment models, increasing transparency around drug pricing, and exploring new approaches to drug development that prioritize patient needs and access to care.

These are amazing stories, and I am delighted these children were able to receive treatment with Zolgensma. However, the price of this medication needs to be down regulated immediately to help this very small population of children suffering from this disease. It really violates the ethical belief of justice because it can make it unequally available for other individuals while others cannot access that treatment whether it be due to inadequate care or lack of finances/health insurance.

😳😘☺️😎😎❤️💜💜💕

India is working on it and will deliver a cheaper alternative for the world and future generations.

Is this medicine can cure MMA disorder.

wtf is pound$

If u are korean, this medicine is almost for free from now on in korea

Who the hell can afford paying 2.5 mln usd though? Is it a medicine for rich people?

In India please where we will get

Happy to hear this news

I am happy to see that the baby is on his way to recovery. Feel sorry for my nephew who is suffering from the same disease, unfortunately we can't afford such expensive treatment.

This is amazing.

money money money money. How about investing that sum of money to make an alternative and providing it for free.

It’s actually not affordable for everyone…like the the Indian baby who is dealing with same deficiency… and I reckon if we can subsidise for the people in need… WE MAY BE ABLE TO SAVE MORE BABIES 👶 AROUND THE GLOBE 🌎🙏🙏🙏

I would never 👎 watch a baby die I would make so much of that drug and give any baby who needs it for free shame on you people try n charge for that drug 😔